Rare Diseases

Rare Diseases in Europe

While an individual disease might be labeled as “rare”, the total number of persons in Europe suffering from identified rare diseases is large.
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Orphan Medicines in Europe

Finding effective treatment for a patient with one of the 6,000 rare diseases can be very difficult.
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Rare Disease Day

The 28th of February, 2019 will be the twelfth international Rare Disease Day coordinated by EURORDIS. On and around this day hundreds of patient organizations from countries and regions all over the world will hold awareness-raising activities.

EffRx supports Eurordis, the organizer of Rare Disease Day, in making the voice of rare diseases heard.