Rare Diseases

Rare Diseases in Europe

While an individual disease might be labeled as “rare”, the total number of persons in Europe suffering from identified rare diseases is large.
Read more

Orphan Medicines in Europe

Finding effective treatment for a patient with one of the 6,000 rare diseases can be very difficult.
Read more

Rare Disease Day

The 29th of February, 2020 will be the 13th international Rare Disease Day coordinated by EURORDIS – Rare Diseases in Europe. Rare Disease Day is to raise awareness for rare diseases and their impact on the lives of patients and families.

On and around this day, hundreds of patient organizations from countries and regions all over the world will hold awareness-raising activities.

EffRx supports Eurordis, the organizer of Rare Disease Day, in making the voice of rare diseases heard.

To get involved, visit rarediseaseday.org to find an event near you or to download communication materials.