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Skip to content
About Us
About EffRx
Business Strategy
Management Team
Board of Directors
Investors
Therapeutic Areas
Adrenal Insufficiency
Adrenal Insufficiency
Congenital Adrenal Hyperplasia
Cystic Fibrosis
Cystic Fibrosis
Unmet Medical Need
Lysosomal Storage Disorders
Gaucher Disease
Niemann-Pick Disease Type C
Osteoporosis
What is Osteoporosis?
Unmet Medical Need
The Adherence Gap
Products & Pipeline
Products
Binosto
®
Alkindi
®
Miglustat
Pipeline
Pipeline Overview
Bronchitol
®
Efmody
®
Business Development
Rare Diseases
Rare Diseases in Europe
Orphan Medicines in Europe
European Market
Affiliations
World Orphan Drug Alliance (WODA)
Newsroom
Press Releases
News
Locations
EffRx Pharmaceuticals | EffRx
